Gene Therapy & Rare Diseases with Assoc. Prof Leszek Lisowski (449)
In this episode, we speak with Associate Professor Leszek Lisowski, Head of the Translational Vectorology Unit at the Children's Medical Research Institute (CMRI), about the cutting-edge world of gene therapy. He explains how viral vectors are engineered to deliver life-saving treatments for rare genetic diseases - many of which are so uncommon, they're only known by the name of the affected gene. Despite being often overlooked, genetic diseases impact 10% of adults and 30% of children in hospitals. Leszek sheds light on the challenges of diagnosis, the promise of emerging genetic testing, and how his work is paving the way for more accurate, effective therapies.
Linkedin: Children's Medical Research Institute, Leszek Lisowski
Facebook: @jeansforgenes
Instagram: @jeansforgenesau
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- Gene Therapy & Rare Diseases with Assoc. Prof Leszek Lisowski (449)
Gene Therapy & Rare Diseases with Assoc. Prof Leszek Lisowski (449)
Oct 25, 2025
In this episode, we speak with Associate Professor
Leszek Lisowski, Head of the Translational Vectorology Unit at the
Children’s Medical Research Institute (CMRI), about the
cutting-edge world of gene therapy. He explains how viral vectors
are engineered to deliver life-saving treatments for rare genetic
diseases - many of which are so uncommon, they’re only known by the
name of the affected gene. Despite being often overlooked, genetic
diseases impact 10% of adults and 30% of children in hospitals.
Leszek sheds light on the challenges of diagnosis, the promise of
emerging genetic testing, and how his work is paving the way for
more accurate, effective therapies.
Linkedin: Children's Medical Research Institute,
Leszek Lisowski
Facebook: @jeansforgenes
Instagram: @jeansforgenesau
About the Podcast
Dr Karl’s a curious optimist – a great combination for a science lover. Join him and his guests for weird facts, amazing conversation and remember, it’s never too late for a happy childhood.
https://drkarl.com/
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